Found 116 matching trials
Part B- G1X-CGD (Lentiviral Vector Transduced CD34+ Cells) in Patients With X-Linked Chronic Granulomatous Disease
PHASE1Background:
X-Linked Chronic Granulomatous Disease (X-CGD) is caused by a ...
Status
Enrolling By Invitation
Location
National Institutes of Health Clinical Center
Lentiviral Gene Therapy for X-Linked Chronic Granulomatous Disease (X-CGD)
PHASE1Chronic Granulomatous Disease (CGD) is a rare inherited disorder in which p...
Location
Great Ormond Street Hospital for Children NHS Trust
Gene-Modified Stem Cell Therapy for Children With Autosomal Recessive Osteopetrosis (ARO)
PHASE1This is a non-randomized, one-arm, open label, single-center, phase I/II, p...
Location
Ospedale San Raffaele
CSL200 Gene Therapy in Adults With Severe Sickle Cell Disease
PHASE1This is a phase 1 pilot study of CSL200 in adult subjects with severe sickl...
Location
City of Hope Medical Center
Study of Gene Therapy Using a Lentiviral Vector to Treat X-linked Chronic Granulomatous Disease
PHASE1Chronic Granulomatous Disease (CGD) is an inherited immunodeficiency disord...
Location
University of California, Los Angeles (UCLA)
Gene-Modified HIV-Protected Stem Cell Transplant in Treating Patients With HIV-Associated Lymphoma
PHASE1This clinical trial studies gene-modified, human immunodeficiency virus (HI...
Location
Fred Hutch/University of Washington Cancer Consortium
Gene Therapy and Chemotherapy in Treating Patients With Advanced Solid Tumors or Non-Hodgkin's Lymphoma
PHASE1RATIONALE: Gene therapy may improve the body's ability to fight cancer or m...
Location
Ireland Cancer Center at University Hospitals Case Medical Center, Case Comprehensive Cancer Center
Retroviral Insertion Site Methodology Study
PHASE4Adenosine deaminase (ADA) is an enzyme involved in the development and func...
Location
Multiple Locations
Gene Therapy for Fanconi Anemia, Complementation Group A
PHASE2The objective of this study is to assess the therapeutic efficacy of a hema...
Status
Active Not Recruiting
Location
Stanford University
Long Term Safety Follow up of Haematopoietic Stem Cell Gene Therapy for the Wiskott Aldrich Syndrome
PHASE1An open follow up study of patients enrolled in the Phase 1/2 clinical tria...
Status
Active Not Recruiting
Location
Hopital Necker - Enfants Malades